Tern Therapeutics have published a press release and written a community letter to update you on their progress in the TTX-381 and TTX-181 clinical trials. These are AAV9 based gene therapies, TTX-381 is looking to address vision loss and has…
We are delighted to announce that Sarah Kenrick has formally joined the BDFA team as our ‘Head of Support and Advocacy’ from 1st February. Sarah has been providing support and advocacy for families over the last 18 months as a…
