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BioMarin CLN2 (Late Infantile Trial) – Evelina London Children’s Hospital

The Evelina London Children’s Hospital, Guy’s and St Thomas’ NHS Foundation Trust, London has begun recruiting subjects with late infantile CLN2 disease, a form of Batten disease, for a clinical trial.  The trial will examine whether BMN190, an experimental drug,…

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The BDFA Welcome A New Member To Our Advisory Team

The BDFA are delighted to welcome Professor Paul Gissen to our team of Medical and Scientific Advisors. Professor Gissen is a Consultant in Inherited Metabolic Diseases (IMDs) at Great Ormond Street Hospital for Children, London, UK and a Wellcome Trust Senior Research…

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